APBD RESEARCH FOUNDATION

Supporting individuals and families affected by Adult Polyglucosan Body Disease (APBD), and accelerating improved APBD diagnoses, care and treatment options.

• Diseases, Disorders, Medical Disciplines N.E.C.

• 38.

LYMPHANGIOMATOSIS & GORHAMS DISEASE ALLIANCE INC

Patient-driven solutions for complex lymphatic anomalies: GLA, GSD, KLA, CCLA • Support-Research-Education • Somatic mutations PIK3/mTor & RAS/MAPK pathways Patient advocacy group dedicated to patient driven solutions for complex lymphatic anomalies We connect patients and families to peers and networks of care, partner to advance new research, and educate the medical community to help all people navigating complex lymphatic anomalies have hope for a healthier tomorrow.

THE PARENT PROJECT FOR MUSCULAR DYSTROPHY RESEARCH INC

Let's advance the research evolution. #EndDuchenne Our mission is to end Duchenne.

Cloves Syndrome Community

Support, Research & Education to improve the quality of life for ppl with CLOVES.

• Fund Raising and/or Fund Distribution

• 41.

Opentreatments Foundation

Our mission is to build software to solve fundamental problems in the society preventing rare diseases from getting treatments.

• Alliance/Advocacy Organizations

• 42.

Haystack Project Inc

We are committed to the Ultra Rare Disease Community.

• Human Services - Multipurpose & Other N.E.C.

• 43.

Atrx Research Alliance

ATRX Research Alliance is a global community dedicated to improving the quality of life of those affected by ATRX syndrome and accelerating research to find treatment.

• Patient Services�Entertainment, Recreation

• 44.

One Rare Inc

One Rare is a non-profit, 501(c)(3) organization based in Massachusetts.

• Specifically Named Diseases

• 45.

FOUNDATION FOR PRADER-WILLI

Foundation for Prader-Willi Research focused on treatments & cure for PWS Our Research FPWRs research programs aim to develop new therapies that will improve the health and wellbeing of those with PWS.