• Diseases, Disorders, Medical Disciplines N.E.C.

• 64.

RASOPATHIES NETWORK USA

A 501c3 organization; Our mission is to advance research of the #RASopathies by bringing stakeholders together.

Odylia Therapeutics Inc

Nonprofit biotech accelerating drug development for #rarediseases.

• Birth Defects, Genetic Diseases

• 66.

Shwachman-Diamond Syndrome Alliance Inc

Shwachman-Diamond Syndrome Alliance is a nonprofit aimed at accelerating research and therapy development for this rare disease.

Young Onset Parkinsons Network

Young Onset Parkinson’s Network is a nonprofit, educational, and charitable organization for those diagnosed with Young Onset Parkinson’s Disease (YOPD) as well as the individuals related to and/or caring for those with the disease.

• Alliance/Advocacy Organizations

• 68.

Rare Melanin Inc

Amplifying Black Experiences in Rare Disease: Your Voice, Our Mission | WE’RE ON A X HIATUS, COME FOLLOW US ON TIKTOK, INSTAGRAM AND THREADS Health is more than absence of disease it is about economics education environment empowerment and community.

Rarekc Foundation

Our mission is to drive innovation in the diagnosis, care and treatment of rare diseases by connecting and inspiring our community.

• Public Foundations

• 70.

TNPO2 Foundation

TNPO2 FOUNDATION WORKED TO ACCELERATE ACCESS TO A CURE FOR ANY "N-OF-1" PATIENT.

• Birth Defects, Genetic Diseases

• 71.

HNRNP FAMILY FOUNDATION

Nonprofit dedicated to serving those impacted by HNRNP-Related Rare Neurodevelopmental Disorders through supporting community and research Home Donate Events Learn Projects Join our Registry Join our Researcher Registry Shop Contact and Connect Submit your story HNRNPC Item HNRNPH1RNDD HNRNPH2RNDD More Our Mission The HNRNP Family Foundation is dedicated to improving the lives of patients and families around the world that live with rare HNRNPRelated Neurodevelopmental Disorders HNRNPRNDDs.

• Specifically Named Diseases Research

• 72.

Dion Foundation for Children with Rare Diseases Inc

Support research. Find a cure. Help children and families fight rare diseases.