• Fund Raising and/or Fund Distribution

• 19.

RARE GENOMICS INSTITUTE INC

RGI is a non-profit organization that provides research to families in need of diagnosis & treatment for rare genetic diseases.

Little Hercules Foundation

We serve the rare disease community through access advocacy and good policy.

• Diseases, Disorders, Medical Disciplines N.E.C.

• 21.

Rare Genes Movement

Our vision is to see every child have access to proper medical, therapeutic, and educational resourc Our purpose is to raise awareness and funds to help families of children with rare genetic disorder.

CureSHANK

CureSHANK's mission is to accelerate the development of treatments and cures for Phelan-McDermid Syndrome and other SHANK-related disorders.

• Fund Raising and/or Fund Distribution

• 23.

Undiagnosed Diseases Network Foundation (UDNF)

Improving access to diagnosis, research, and care for all with undiagnosed and ultra-rare conditions.

• Alliance/Advocacy Organizations

• 24.

Rare Disease Company Coalition Inc

We are a coalition of life science companies committed to discovering, developing & delivering rare disease treatments for the patients we serve.

• Alliance/Advocacy Organizations

• 25.

KIF1A.ORG

We connect families affected by KIF1A and relentlessly work to accelerate research.

• Fund Raising and/or Fund Distribution

• 26.

CURE RARE DISEASE INC

Nonprofit biotech leading a global collaboration to develop life-saving medicines for rare diseases Revolutionizing UltraRare Disease Treatment through Innovation and Collaboration Revolutionizing UltraRare Disease Treatment through Innovation and Collaboration What Wex27re Working Towards We envision a future where every patient has access to treatment.

• Cancer Research

• 27.

TargetCancer Foundation Inc

TargetCancer Foundation (TCF) works to advance the development of more effective & personalized treatments for people with rare cancers.