JEFFREY MODELL FOUNDATION

The Jeffrey Modell Foundation is a global nonprofit organization dedicated to Advocacy Research Education Awareness Newborn Screening and Genetic Sequencing for Primary Immunodeficiency.

Smith-Lemli-Opitz Foundation

The Smith-Lemli-Opitz Foundation is a non-profit organization dedicated to supporting families, individuals and professionals dealing with Smith-Lemli-Opitz.

• Fund Raising and/or Fund Distribution

• 300.

HUNTER SYNDROME FOUNDATION

The Hunter Syndrome Foundation is a 501(c)3 non-profit corporation with a mission to fund potential therapies that will ultimately find a cure for this disorder.

• Specifically Named Diseases

• 301.

NATIONAL UREA CYCLE DISORDERS FOUNDATION

Nonprofit supporting patients & families affected by urea cycle disorders.

• Fund Raising and/or Fund Distribution

• 302.

Patrick Allen Melvin Foundation

Partnering with nonprofit organizations and charities to raise funds and awareness for their cause.

OPMD Association

Advocates for Oculopharyngeal Muscular Dystrophy.

• Birth Defects, Genetic Diseases

• 304.

Green Ivy Health Inc

WE HELP PATIENTSFIGHT vEDS FIGHT vEDS is a nonprofit organization dedicated to fighting and finding a treatment for vascular EhlersDanlos Syndrome.

• Fund Raising and/or Fund Distribution

• 305.

Destroy Duchenne

Destroy Duchenne‘s mission is to Complete the Cure™ for Duchenne muscular dystrophy by advancing gene-editing and gene therapy technologies into human practice.

• Specifically Named Diseases

• 306.

Project CASK

An innovative rare disease non-profit driving breakthroughs in treatments and a cure for CASK gene disorders.