BEYOND BATTEN DISEASE FOUNDATION

Mission: eradicate Batten disease. Batten disease is a fatal neurodegenerative disorder that takes away childhood, and then takes away.

• Brain Disorders

• 344.

VANISHING WHITE MATTER FOUNDATION

Our mission is to raise funds to support VWM Leukodystrophy specific research to help treat and cure this rare disease.

• Birth Defects, Genetic Diseases

• 345.

Turners Syndrome Society of the United States

Official twitter page for Turner Syndrome Society of the US, where we advance knowledge, facilitate research and providing support for all touched by TS.

Turner Syndrome Society of the United States

Official twitter page for Turner Syndrome Society of the US, where we advance knowledge, facilitate research and providing support for all touched by TS.

American Syringomyelia Alliance Project, Inc.

ASAP's mission: "to improve the lives of persons affected by Syringomyelia, Chiari Malformation and related disorders while we find the cure.

CureSHANK

CureSHANK's mission is to accelerate the development of treatments and cures for Phelan-McDermid Syndrome and other SHANK-related disorders.

• Medical Specialty Research

• 349.

The American Porphyrias Expert Collaborative Inc

TO PROMOTE AND CARRY OUT RESEARCH, AND PROMOTE EDUCATIONAL ACTIVITIES, REGARDING PORPHYRIAS AND HEME BIOSYNTHESIS THROUGH DEVELOPMENT OF BEST PRACTICES, RESEARCH SUPPORT, AND EDUCATION.

• Medical Specialty Research

• 350.

FIBROMUSCULAR DYSPLASIA SOCIETY OF

The recognized leader in the support of Fibromuscular Dysplasia (FMD) awareness, education and research.

• Fund Raising and/or Fund Distribution

• 351.

TO CURE A ROSE FOUNDATION

At To Cure A Rose Foundation, we’re on a mission to make genetic treatments faster, more affordable, and within reach—so that the next child born with a rare disease can receive a customized drug within days of diagnosis.