• Birth Defects, Genetic Diseases

• 37.

Gene Spotlight Inc

We are a nonprofit medical research and advocacy organization committed to spark breakthroughs in treatments and cures for rare genetic disorders, including lysosomal storage diseases, uncommon cancers and other orphan diseases.

Rare Trait Hope Fund

Rare trait Hope Fund facilitates research and provides funding for the development of treatments for a rare disease called Aspartylglucosaminuria (AGU) in hopes to save lives of AGU kids and adults.

• Brain Disorders

• 39.

Global Coalition for Adaptive Research Inc

GCAR is a 501(c)(3) nonprofit organization accelerating the discovery and development of treatments for patients with rare and deadly diseases Global Coalition for Adaptive Research (GCAR) is a nonprofit organization committed to accelerating the discovery and development of treatments for patients with rare and deadly diseases Our mission is to speed the discovery and development of treatments for patients with rare and deadly diseases by serving as the sponsor of innovative trials.

• Alliance/Advocacy Organizations

• 40.

Haystack Project Inc

We are committed to the Ultra Rare Disease Community.

• Fund Raising and/or Fund Distribution

• 41.

The Children's Rare Disorders Fund

Dedicated to curing rare genetic disorders Founded in July 2022 by parents of a toddler affected by FOXG1, The CRD Fund focuses on under served communities in the rare disorder space.

• Birth Defects, Genetic Diseases Research

• 42.

Channeling Hope Foundation

Channeling Hope Foundation A community of researchers and families driven to advance care and develop treatments for those affected by NALCNrelated disorders.

• Patient Services�Entertainment, Recreation

• 43.

One Rare Inc

One Rare is a non-profit, 501(c)(3) organization based in Massachusetts.

COALITION FOR 21ST CENTURY MEDICINE

REGULATORY REIMBURSEMENT INTELLECTUAL PROPERTY Advanced Diagnostics Are Key to the Future of Quality Affordable Healthcare The Coalition for 21st Century Medicine represents some of the worlds most innovative diagnostic technology companies clinical laboratories researchers physicians venture capitalists and patient advocacy groups all linked by a common mission to develop and make available stateoftheart diagnostics that improve patient health.

• Educational Services and Schools - Other

• 45.

MISSION CURE INC

A new model for curing disease, starting with pancreatitis.