• Private Grantmaking Foundations

• 28.

Jain Foundation Inc

The Jain Foundation's mission is to identify treatments for Dysferlinopathy also known as LGMD2B/R2 or Miyoshi Myopathy ORCHESTRATING A CURE FOR DYSFERLINOPATHY The Jain Foundation is singularly focused on finding a cure for dysferlinopathy also referred to as LGMD2B LGMDR2 Miyoshi Myopathy 1 ORCHESTRATINGA CURE FORDYSFERLINOPATHY The Jain Foundation is singularly focused on finding a cure for dysferlinopathy also referred to as LGMD2B LGMDR2 Miyoshi Myopathy 1 WHAT IS DYSFERLINOPATHY.

THE NEUROMUSCULAR DISEASE FOUNDATION

NDF is a nonprofit whose mission is to raise awareness and encourage testing for HIBM and to find a cure for neuromuscular diseases, including HIBM.

FAMILIAL DYSAUTONOMIA NOW FOUNDATION

FD NOW is a 501c3 non-profit organization dedicated to funding the fast-track research at the Laboratory for Familial Dysautonomia Research at Fordham University in New York, USA.

Foundation for Angelman Syndrome Therapeutics

FAST is the premier patient advocacy organization working to cure Angelman syndrome.

Little Hercules Foundation

We serve the rare disease community through access advocacy and good policy.

• Birth Defects, Genetic Diseases

• 33.

Uba5 Foundation

This page is to help raise awareness and connect with others that have been diagnosed UBA5 gene mutation.

• Fund Raising and/or Fund Distribution

• 34.

COALITION TO CURE CALPAIN 3

Coalition to Cure Calpain 3 (C3) has a pinpoint focus: to drive research towards a cure for limb-girdle muscular dystrophy type 2A (LGMD2A/R1, a form of Calpainopathy).

• Heart and Circulatory

• 35.

Wittek Research Foundation for Hypertrophic Cardiomyopathy Inc

Dedicated to supporting research that will transform the prevention, diagnosis, and treatment of Hypertrophic Cardiomyopathy Dedicated to supporting research that will transform the prevention diagnosis and treatment of HCM Learn More Our Goals Our goal is to promote rapid identification and development of new innovative treatments for Hypertrophic Cardiomyopathy that will modify or eradicate the disease.

• Nerve, Muscle, and Bone Diseases

• 36.

Cure VCP Disease Inc

Promoting a cure for diseases related to mutations of the Valosin Containing Protein gene ABOUT US FOR PATIENTS FOR RESEARCHERS FOR CLINICIANS EVENTS BLOG GIVE SHOP MORE Finding a cure is in our DNA Cure VCP Disease Inc.