Cure SMA

Funding groundbreaking research for SMA.

• Fund Raising and/or Fund Distribution

• 29.

HUNTER SYNDROME FOUNDATION

The Hunter Syndrome Foundation is a 501(c)3 non-profit corporation with a mission to fund potential therapies that will ultimately find a cure for this disorder.

• Specifically Named Diseases Research

• 30.

GRACE SCIENCE FOUNDATION

We are changing how scientific research is done.

• Fund Raising and/or Fund Distribution

• 31.

Ellie White Foundation for Rare Genetic Disorders Inc

We will not give up until a cure for Wolfram syndrome is found for Ellie and the children suffering from this disorder.

Coming Together For A Cure, Inc

A 501c3 nonprofit dedicated to advancing stem cell therapy for Duchenne MD and other rare diseases.

Foxg1 Research Foundation

FOXG1 syndrome is a childhood neurological genetic disorder and is a key to understanding many brain disorders.

• Fund Raising and/or Fund Distribution

• 34.

The TBCD Foundation

The TBCD Foundation is a non-profit organization for and by the TBCD Disorder community to raise funds and awareness in order to pursue effective treatments and a cure for TBCD.

• Birth Defects, Genetic Diseases Research

• 35.

International FOXP1 Foundation

Our mission is to build a global community that empowers and supports families and individuals with FOXP1 syndrome by sharing knowledge, inspiring hope, supporting research, and raising awareness.

• Specifically Named Diseases

• 36.

CTNNB1 Connect and Cure Inc

Connecting families, raising awareness, finding treatments and a cure for CTNNB1 Syndrome 🧬💛💙 https://t.