• Birth Defects, Genetic Diseases

• 163.

Southeastern Rett Syndrome Alliance

TO DEVELOP UNDERSTANDING AND AWARENESS OF RETT SYNDROME; TO PROMOTE THE GENERAL WELFARE OF THOSE WITH RETT SYNDROME; TO ASSIST IN IDENTIFYING PERSONS WITH RETT SYNDROME; TO SUPPORT FAMILIES IN COPING WITH THE DISORDER, AND CONDUCT ACTIVITIES AIMED AT PREVENTION, TREATMENT AND ERADICATION OF RETT SYNDROME Be sure to grab some Awareness Items in the Research Dr.

• Research Institutes and/or Public Policy Analysis

• 164.

International Pnh Interest Group

Cookie settings Save the Date. Paris France ESHEBMTEHAIPIG 3rd Translational Research Conference Bone Marrow Failure and Leukemia Predisposition Syndromes IPIG Friday Satellite Symposium at ASH Annual Meeting Exposition Our mission The mission of the International PNH Interest Group is to advance optimal treatment and care of people living with paroxysmal nocturnal hemoglobinuria PNH and related conditions to provide instruction information and training to health care providers and to help further research on new and effective treatment options and improved patient access to approved therapies and treatments.

• Specifically Named Diseases

• 165.

Prion Alliance Inc

Non-profit organization devoted to funding scientific research towards a treatment or cure for human prion diseases.

Aplastic Anemia and MDS International Foundation

Aplastic Anemia and MDS Int'l Found supports patients & families with #aplastic anemia, #MDS, #PNH, and related bone marrow failure diseases #AML #PRCA #CMML Fighting Bone Marrow Failure Diseases through Patient Support and Research -Aplastic Anemia, MDS, PNH The Aplastic Anemia & MDS International Foundation empowers individuals diagnosed with aplastic anemia, myelodysplastic syndrome (MDS), paroxysmal nocturnal hemoglobinuria (PNH) and their support network by providing timely information, a community of support, improved treatment through health provider education, and hope for a cure through promotion of research.

• Birth Defects, Genetic Diseases Research

• 167.

Sanfilippo Hope Initiative

Jarod and Caleb are brothers who suffer from an ultra-rare disease called Sanfilippo Syndrome.

Vasculitis Foundation

Awareness. Support. Research. http://www.

CONNECT1D

The mission of ConnecT1D is to connect people whose lives are affected by Type 1 Diabetes through programs, social networking, educational meetings and support activities at every stage of their lives.

HISTIOCYTOSIS ASSOCIATION INC

Dedicated to raising awareness about histiocytic disorders, providing educational and emotional support, and funding research.

• Single Organization Support

• 171.

THE MED13L FOUNDATION INC

Supporting MED13L families through awareness, research, and community.