• Birth Defects, Genetic Diseases

• 154.

NATIONAL TAY SACHS & ALLIED DISEASES ASSOCIATION INC

National Tay-Sachs & Allied Diseases Association (NTSAD) leads the worldwide fight to treat and cure Tay-Sachs, Canavan, GM1, and Sandhoff diseases.

• Fund Raising and/or Fund Distribution

• 155.

Parkinson Alliance, Inc

Founded in 1999, The Parkinson Alliance is a national nonprofit organization, in partnership with The Tuchman Foundation.

• Specifically Named Diseases Research

• 156.

Coalition Duchenne

We're on a mission to do everything FUN to raise global awareness for Duchenne muscular dystrophy, to fund research for a cure.

The NVLD Project

We are a non-profit organization that is raising awareness and building support for children, adolescents and adults with #NVLD.

• Professional Societies & Associations

• 158.

Plasma Protein Therapeutics Association

The European division of @plasmaproteins, where we engage with policymakers & patients in 🇪🇺, to advocate for patient access to #plasma-derived therapies.

• Fund Raising and/or Fund Distribution

• 159.

COALITION TO CURE CALPAIN 3

Coalition to Cure Calpain 3 (C3) has a pinpoint focus: to drive research towards a cure for limb-girdle muscular dystrophy type 2A (LGMD2A/R1, a form of Calpainopathy).

• Specifically Named Diseases

• 160.

Jansens Foundation

Founder & Executive Director of The Jansen's Foundation.

CMT Research Foundation Inc

The CMT Research Foundation has one mission: Deliver treatments and cures for #CMT.

• Fund Raising and/or Fund Distribution

• 162.

A Noble Journey Inc

Our mission is to raise money for the awareness of treatment of and research for a cure of MPS.