• Birth Defects, Genetic Diseases Research

• 109.

Cure CMD

Cure CMD’s mission is to advance research toward treatments for congenital muscular dystrophies and empower those living with CMD.

• Public Health Programs

• 110.

United Pompe Foundation

SUPPORT RESEARCH FOR POMPE DISEASE AND HELP PATIENTS DEALING WITH POMPE DISEASE United Pompe Foundation The United Pompe Foundation was formed to assist patients andor their families with medical costs and other expenses that these patents and families face and may not be able to cover or fully cover through their insurance.

THE CLINIC FOR SPECIAL CHILDREN INC

A nonprofit comprehensive medical practice focused on treating & researching rare genetic disorders.

• Fund Raising and/or Fund Distribution

• 112.

GRACE ROSE FOUNDATION

Grace Rose is a young girl living with Cystic Fibrosis.

• Single Organization Support

• 113.

Organic Acidemia Association Corporation

The Organic Acidemia Assn, our mission is to support families, share awareness of organic acid disorders, fund research for better treatments & advocate NBS.

• Specifically Named Diseases Research

• 114.

Plasminogen Deficiency Foundation

A 501(c)(3) public charity dedicated to improving the lives of patients with plasminogen deficiency (PLGD).

Cure Pogz Disorders Foundation Inc

The ‘Cure Pogz Disorders Foundation’ ( CPDF) Mission is to urgently improve the lives of individuals and families affected by POGZ gene disorders by funding and accelerating cutting-edge science to discover treatments integral to our Path to Cure.

• Diseases, Disorders, Medical Disciplines N.E.C.

• 116.

Rare Genes Movement

Our vision is to see every child have access to proper medical, therapeutic, and educational resourc Our purpose is to raise awareness and funds to help families of children with rare genetic disorder.

• Fund Raising and/or Fund Distribution

• 117.

GLUT1 DEFICIENCY FOUNDATION INC

Building a brighter future Bringing help and hope to the Glut1 Deficiency community as we work together to improve lives through awareness education advocacy and research Shining a light on Glut1 Deficiency Glucose Transporter Protein Type 1 Deficiency Syndrome Glut1 Deficiency is a rare genetic condition that impairs brain metabolism.