Race for Adam Foundation

Adam Recke was diagnosed in 2005 with an extremely rare, degenerative terminal disease, Type-C Niemann-Pick Syndrome.

Coming Together For A Cure, Inc

A 501c3 nonprofit dedicated to advancing stem cell therapy for Duchenne MD and other rare diseases.

Kcnq2 Cure Alliance Inc

Our promise is to educate and to advance research leading to treatments or a cure for patients living with the genetic disorder KCNQ2 Raising awareness, educating, and advancing research for KCNQ2 Developmental and Epileptic Encephalopathy.

• Epilepsy

• 4.

Kcna2 Epilepsy Inc

Join the KCNA2 Epilepsy Global Support Community on our quest for more information, research, treatments and a cure.

Kruzn for A Kure Foundation

Kruzn For A Kure Foundation is a non-profit organization funding research for an extremely rare genetic disease & fatal type of dwarfism, #SIOD.

• Specifically Named Diseases

• 6.

Smith-Kingsmore Syndrome Foundation

Smith-Kingsmore Syndrome is a rare genetic disease.

• Epilepsy

• 7.

Kcnt1 Slack Epilepsy Foundation Inc

Variants in the KCNT1 gene cause drug-resistant seizures.

• Patient Services�Entertainment, Recreation

• 8.

Idefine Inc

IDefine is committed to identifying life-changing treatments & cures and building community for those with Kleefstra Syndrome and intellectual disabilities.

• Specifically Named Diseases

• 9.

CTNNB1 Connect and Cure Inc

Connecting families, raising awareness, finding treatments and a cure for CTNNB1 Syndrome 🧬💛💙 https://t.