GALACTOSEMIA FOUNDATION

A national, nonprofit, volunteer organization providing information, support and networking opportunities to those impacted by galactosemia since 1985 Galactosemia Foundation is a national, non-profit, volunteer organization whose mission is to provide information, support, and networking opportunities to families affected by galactosemia.

• Alliance/Advocacy Organizations

• 74.

PCD KS FOUNDATION

Working together to find a cure and improve care for those with ciliary disorders and their families by increasing awareness, research and support.

Cystinosis Research Foundation

The Cystinosis Research Foundation’s (CRF) mission is to find better treatments and a cure for cystinosis, a rare genetic disease that destroys every organ.

• Birth Defects, Genetic Diseases Research

• 76.

Sanfilippo Hope Initiative

Jarod and Caleb are brothers who suffer from an ultra-rare disease called Sanfilippo Syndrome.

• Birth Defects, Genetic Diseases Research

• 77.

Fam177a1 Research Fund

Founder and President, FAM177A1 Research Fund The mission of the FAM177A1 Research Fund is to improve the lives of those affected by FAM177A1 Associated Disorder through research and development of transformative therapies.

• Alliance/Advocacy Organizations

• 78.

Ctx Alliance NFP

Providing education, support, advocacy, and promoting research for CTX patients, their families, and medical professionals who treat and study this rare disease Providing education, support, advocacy, and promoting research for CTX patients, their families, and medical professionals who treat and study this rare disease.

HALITE SOLUTIONS GROUP

Supporting the health and social needs of individuals with cystic fibrosis.

• Adult, Continuing Ed

• 80.

TEXAS LIVER INSTITUTE INC

The Texas Liver Institute (TLI) is a non-for-profit organization dedicated to fighting liver disease.

• Kidney

• 81.

INTERNATIONAL SOCIETY OF GLOMERULAR

THE INTERNATIONAL SOCIETY OF We envision a future where all people with glomerular kidney disease can access accurate early diagnosis and suitable treatment to preserve the health of their kidneys.