• Brain Disorders

• 73.

National Organization of Disorders of the Corpus Callosum

The NODCC is the leading nonprofit dedicated to providing education and enhancing lives of those with disorders of the corpus callosum.

Rett Syndrome Research Trust, Inc.

Fighting to cure Rett Syndrome and MECP2 related disorders.

Cystinosis Research Foundation

The Cystinosis Research Foundation’s (CRF) mission is to find better treatments and a cure for cystinosis, a rare genetic disease that destroys every organ.

Coming Together For A Cure, Inc

A 501c3 nonprofit dedicated to advancing stem cell therapy for Duchenne MD and other rare diseases.

• Fund Raising and/or Fund Distribution

• 77.

Eleanor Kaplan Foundation Inc

To raise funds and awareness to develop cures for Ultra Rare Neurodegenerative Diseases.

• Alliance/Advocacy Organizations

• 78.

Charlotte and Gwenyth Gray Foundation

Sisters, Charlotte & Gwenyth, were diagnosed w/ Batten Disease, a rare & fatal brain disease.

• Diseases of Specific Organs

• 79.

THE CALLIOPE JOY FOUNDATION

Mission Contact More Dear Friends and Supporters I am writing to you with a heart full of gratitude and appreciation.

• Birth Defects, Genetic Diseases

• 80.

CACNA1A Foundation

Nonprofit dedicated to a brighter future for those with CACNA1A variants.

• Nonmonetary Support N.E.C.*

• 81.

SPOONBILL FOUNDATION

Finding a solution for PKAN Spoonbill Foundation and our sister organization Stichting Lepelaarwere founded with the goal to discover develop and deliver therapeutics for PKAN and all NBIA disorders in partnership with the NBIA community as swiftly as possible and at the lowest cost.