• Neurology, Neuroscience

• 64.

JB'S KEYS TO DMD INC

Giving boys affected by DMD the opportunity of a lifetime.

• Other Philanthropy, Voluntarism, and Grantmaking Foundations N.E.C.

• 65.

INTERNATIONAL CHILDRENS ANOPHTHALMIA NETWORK INC

ICAN a voluntary not for profit organization, is a group of families and professionals dedicated to lending support to individuals who want to learn more about microphthalmia and anopthalmia and associated genetic counseling.

Coming Together For A Cure, Inc

A 501c3 nonprofit dedicated to advancing stem cell therapy for Duchenne MD and other rare diseases.

• Nerve, Muscle, and Bone Research

• 67.

FSHD Society

World’s largest research-focused patient organization for facioscapulohumeral muscular dystrophy (FSHD).

• Specifically Named Diseases Research

• 68.

Cure Szt2

Cure SZT2 is a non-profit organization dedicated to families affected by the genetic mutation SZT2.

• Fund Raising and/or Fund Distribution

• 69.

COALITION TO CURE CALPAIN 3

Coalition to Cure Calpain 3 (C3) has a pinpoint focus: to drive research towards a cure for limb-girdle muscular dystrophy type 2A (LGMD2A/R1, a form of Calpainopathy).

• Fund Raising and/or Fund Distribution

• 70.

The Children's Rare Disorders Fund

Dedicated to curing rare genetic disorders Founded in July 2022 by parents of a toddler affected by FOXG1, The CRD Fund focuses on under served communities in the rare disorder space.

• Birth Defects, Genetic Diseases

• 71.

STXBP1 FOUNDATION

Non-profit dedicated to ending STXBP1-related disorders, rare neurodevelopmental and epileptic encephalopathies, and spreading awareness of this rare disease.

• Specifically Named Diseases

• 72.

FOUNDATION FOR PRADER-WILLI

Foundation for Prader-Willi Research focused on treatments & cure for PWS Our Research FPWRs research programs aim to develop new therapies that will improve the health and wellbeing of those with PWS.