• Public Foundations

• 55.

BARTH SYNDROME FOUNDATION INC

Barth Syndrome Foundation - saving lives through education, advances in treatments, and finding a cure for Barth syndrome.

• Birth Defects, Genetic Diseases

• 56.

Tennessee Prader-Willi Association, Inc.

We provide support and information for people with PWS & their families.

• Birth Defects, Genetic Diseases

• 57.

International Rett Syndrome Association, Inc.

We are transforming lives every day in our fight to treat and cure Rett syndrome and better the lives of families living with this devastating disorder.

• Specifically Named Diseases

• 58.

ASSOCIATION FOR GLYCOGEN STORAGE DISEASE

Created for support and awareness of the various types of Glycogen Storage Disease.

• Fund Raising and/or Fund Distribution

• 59.

Birds for Sofia Inc

We support children diagnosed with rare, inheritable diseases from Eastern Europe.

• Management & Technical Assistance

• 60.

Pathways Corp

To elevate the patient's voice to increase access to care and eliminate bias by bringing stakeholders together Home Our Team Events Initiatives Partners Media Kit Contact More Its Time to Listen to the Rare Disease Community.

• Specifically Named Diseases

• 61.

Watch 4 Wegeners

It could save a life. Home Sarahx27s Story About Our Board Contact Us Run To Raise Testimonials More Watch 4 Wegeners It Could Save a Life Our daughter Sarah River Whitmire was a college student in pharmacy school when she died suddenly at age 20 from complications of undiagnosed Granulomatosis with Polyangiitis GPA also known as Wegener39s Disease a rare autoimmune disease that no one knew she had.

United MSD Foundation

Our mission is simple, yet powerful: To cure Multiple Sulfatase Deficiency.

International Rett Syndrome Foundation

We are transforming lives every day in our fight to treat and cure Rett syndrome and better the lives of families living with this devastating disorder.