• Birth Defects, Genetic Diseases Research

• 118.

Ryan's Quest

Fighting for an end for Duchenne muscular dystrophy.

HUNTINGTONS DISEASE YOUTH ORGANIZATION

An international non-profit organisation supporting, educating & empowering young people, up to 35 years, impacted by Huntington’s Disease around the world.

• Specifically Named Diseases

• 120.

Prion Alliance Inc

Non-profit organization devoted to funding scientific research towards a treatment or cure for human prion diseases.

• Birth Defects, Genetic Diseases Research

• 121.

International Society for Cellular Therapy

Driving the translation of cell & gene therapies for the benefit of patients worldwide.

• Birth Defects, Genetic Diseases Research

• 122.

Spata Foundation Inc

Our mission is to advocate, educate, and raise funds for research towards SPATA5 & SPATA5L1 Disorders The SPATA Foundation's Mission is to advocate, educate, and drive research towards SPATA5 and SPATA5L1 Related Disorders.

OPMD Association

Advocates for Oculopharyngeal Muscular Dystrophy.

• Fund Raising and/or Fund Distribution

• 124.

Arid1B Research Foundation

Accelerating the development of disease-modifying treatments for #ARID1B-RD (haploinsufficiency) - the most frequently mutated gene in de novo NDDs (ASD, ID).

• Birth Defects, Genetic Diseases

• 125.

EBF3 HADDS Foundation

EBF3 HADDS FOUNDATION Home SupportDonate About Events Blog Shop More ARTICLES EVENTS BLOG CONNECT Learn more about what is happening globally with our community.

• Birth Defects, Genetic Diseases Research

• 126.

ADLD CENTER

The ADLD Center is focused on raising awareness about Autosomal Dominant Leukodystrophy ADLD and developing a network of clinicians researchers patients and their caregiversadvocates in order to raise funds as we move forward towards finding a cure.