Rare Trait Hope Fund

Rare trait Hope Fund facilitates research and provides funding for the development of treatments for a rare disease called Aspartylglucosaminuria (AGU) in hopes to save lives of AGU kids and adults.

CUREPSP

To raise awareness, build community, improve care and find a cure for PSP, CBD and MSA.

Aplastic Anemia and MDS International Foundation

Aplastic Anemia and MDS Int'l Found supports patients & families with #aplastic anemia, #MDS, #PNH, and related bone marrow failure diseases #AML #PRCA #CMML Fighting Bone Marrow Failure Diseases through Patient Support and Research -Aplastic Anemia, MDS, PNH The Aplastic Anemia & MDS International Foundation empowers individuals diagnosed with aplastic anemia, myelodysplastic syndrome (MDS), paroxysmal nocturnal hemoglobinuria (PNH) and their support network by providing timely information, a community of support, improved treatment through health provider education, and hope for a cure through promotion of research.

• Kidney

• 4.

PKD Foundation

Dedicated to finding treatments and a cure for polycystic kidney disease (PKD).

• Fund Raising and/or Fund Distribution

• 5.

Sdhb Coalition Inc

Our mission is to educate healthcare professionals and patients on the SDHB genetic germline mutation as well as its role and impact in this orphan disease SEE SCHEDULE O ABOVE Vision Mission Our mission is to educate healthcare professionals and patients on the SDHB genetic germline mutation as well as its role and impact in this orphan disease namely Pheochromocytoma and Paraganglioma.

• Fund Raising and/or Fund Distribution

• 6.

Tbc1D24 Foundation

Tbc1d24 foundation is a research organization and connecting site for caregivers, families, and those diagnosed with Tbc1d24 mutations.

CMT Research Foundation Inc

The CMT Research Foundation has one mission: Deliver treatments and cures for #CMT.

• Alliance/Advocacy Organizations

• 8.

Rare Disease Company Coalition Inc

We are a coalition of life science companies committed to discovering, developing & delivering rare disease treatments for the patients we serve.

• Fund Raising and/or Fund Distribution

• 9.

BENEFIT OTHERS FOUNDATION

Helping to overcome hardships and providing opportunities for children and their families Who We Are Benefit Others Foundation is a nonprofit 501c3 organization committed to enriching the lives of others.