• Specifically Named Diseases

• 424.

HEMOCHROMATOSIS INFORMATION SOCIETY

The Hemochromatosis Information Society is a nonprofit organization providing valuable information to patients and physicians concerning hereditary hemochromatosis.

NEUROFIBROMATOSIS INC

Neurofibromatosis (NF) Network is the national non-profit serving individuals affected by neurofibromatosis.

• Single Organization Support

• 426.

Organic Acidemia Association Corporation

The Organic Acidemia Assn, our mission is to support families, share awareness of organic acid disorders, fund research for better treatments & advocate NBS.

• Private Grantmaking Foundations

• 427.

Brian J Kelley Foundation for Hope Inc

Through Brian’s Hope, a 501(c)(3) charitable foundation, we look forward to when no child experiences the devastation of adrenoleukodystrophy (ALD) Through Brian’s Hope, a 501(c)(3) charitable foundation, we look forward to a day when no child will experience the devastation of adrenoleukodystrophy (ALD).

• Birth Defects, Genetic Diseases Research

• 428.

Hope for Pdcd Foundation

Fundraising for a cure for Pyruvate Dehydrogenase Complex Deficiency (PDCD) & advancing research for rare diseases.

• Specifically Named Diseases

• 429.

CURE ADSSL1

501(c)(3) non-profit patient advocacy group with the mission to find treatment for ADSSL1 myopathy Mission of the CURE ADSSL1 organization is to invest in research and develop treatment options for patients with rare neuromuscular disease caused by mutation in ADSSL1 gene.

• Birth Defects, Genetic Diseases Research

• 430.

International FOXP1 Foundation

Our mission is to build a global community that empowers and supports families and individuals with FOXP1 syndrome by sharing knowledge, inspiring hope, supporting research, and raising awareness.

• Public Foundations

• 431.

The Mathew Forbes Romer Foundation Inc

Education & Research of Children's Genetic Diseases of the Brain MFRF was founded in South Florida in 1998 with a mission to prevent and eventually cure fatal children's genetic diseases of the brain.

CHILDREN'S HEALTH FOUNDATION

CHKD is a non-profit children’s hospital promoting health, healing, and hope for all children.