National MPS Society, Inc.

The National MPS Society exists to find cures for MPS and ML.

• Educational Services and Schools - Other

• 425.

International Restless Legs Syndrome Study Group Foundation

THE PURPOSE OF THE ORGANIZATION IS TO PROMOTE THE EDUCATION AND RESEARCH OF SLEEP DISORDERS INCLUDING RESTLESS LEGS SYNDROME.

• Alliance/Advocacy Organizations

• 426.

Team Telomere

An international community for telomere biology disorders.

• Fund Raising and/or Fund Distribution

• 427.

Usher Iii Initiative Inc

Dedicated to developing cures for blindness TO ACHIEVE ITS GOAL OF DEVELOPING A TREATMENT TO SLOW OR REVERSE THE VISION LOSS ASSOCIATED WITH USHER III, THE INITIATIVE HAS PURSUED AN APPROACH THAT FOCUSES ON SMALL MOLECULE CHAPERONE THERAPY.

• Other Medical Research N.E.C.

• 428.

Cgta Research Group

Our mission:1. To bring therapies for rare diseases, involving viral vector delivery of DNA to the CNS by various routes, from late-pre-clinical development through to human trials and to public availability as efficiently as possible.

• Private Independent Foundations

• 429.

Won Sook Chung Foundation

Established in 2012 to increase awareness and acceptance of diagnostic tools and interventions outside the established medical paradigm.

Alpha-1 Foundation, Inc.

Our mission is to increase awareness of and find a cure for Alpha-1 Antitrypsin Deficiency.

• Alliance/Advocacy Organizations

• 431.

Young Genetic Stroke Alliance

Raising awareness and educating the community on all things related to this rare disease.

• Fund Raising and/or Fund Distribution

• 432.

Patrick Allen Melvin Foundation

Partnering with nonprofit organizations and charities to raise funds and awareness for their cause.