• Nerve, Muscle, and Bone Diseases

• 37.

CureDuchenne

We are committed to improving the lives of those affected by Duchenne through accelerating research, improving care and empowering the community.

• Birth Defects, Genetic Diseases

• 38.

Gene Spotlight Inc

We are a nonprofit medical research and advocacy organization committed to spark breakthroughs in treatments and cures for rare genetic disorders, including lysosomal storage diseases, uncommon cancers and other orphan diseases.

NephCure

Fighting for a world where all who are affected by rare, protein-spilling kidney disease are connected to new and better treatments — and one day, a cure.

Lcc Foundation Inc

The LCC Foundation’s MISSION is to help families across the United States and beyond diagnosed with Leukoencephalopathy with Brain Calcifications and Cysts (LCC) by giving them the resources they need to fight this rare and devastating disease.

• Fund Raising and/or Fund Distribution

• 41.

Coopers Cure

COOPER39S CURE HOME DONATE COOPERx27S STORIES COOPER FEST COOPERx27S TRIBE CONTACT More.

• Birth Defects, Genetic Diseases

• 42.

Iqsec2 Research and Advocacyfoundation

Welcome to IQSEC2. ORG Research and Advocacy Foundation MISSION STATEMENT Vision In the next 10 years we will dramatically improve the quality of life for those affected by IQSEC2 mutations through 1 the establishment and dissemination of standard treatment and therapy protocols to medical practitioners and therapists worldwide 2 support of research and development of new and innovative treatments for IQSEC2 related diseases and 3 uplift support all loved ones of those affected by IQSEC2 through an advocate community and its allies.

• Fund Raising and/or Fund Distribution

• 43.

A Noble Journey Inc

Our mission is to raise money for the awareness of treatment of and research for a cure of MPS.

• Nerve, Muscle, and Bone Diseases

• 44.

Cure VCP Disease Inc

Promoting a cure for diseases related to mutations of the Valosin Containing Protein gene ABOUT US FOR PATIENTS FOR RESEARCHERS FOR CLINICIANS EVENTS BLOG GIVE SHOP MORE Finding a cure is in our DNA Cure VCP Disease Inc.

• Patient Services�Entertainment, Recreation

• 45.

HAVEN EILEEN KILEY FOUNDATION INC

501c3 helping children sick or in need and the families and facilities that care for them Haven’s Foundation is a 501(c) 3 non-profit organization founded in 2016, after our precious daughter, Haven Eileen, lost her life to a genetic disease.