LIVE RHYSSTRONG FOUNDATION

Our goal is to help the Spinal Muscular Atrophy community's efforts towards research, family support and awareness of the #1 genetic killer of infants.

• Specifically Named Diseases

• 38.

NATIONAL UREA CYCLE DISORDERS FOUNDATION

Nonprofit supporting patients & families affected by urea cycle disorders.

• Nerve, Muscle, and Bone Diseases

• 39.

Best Day Ever Foundation

Changing lives. one BEST DAY EVER at a time.

• Services to Promote the Independence of Specific Populations

• 40.

Project Strong Inc

Strong missioN Our mission at Project Strong is to empower children and young adults living with neuromuscular diseases discover and express their unique strengths by providing educational programs activities events that meet their needs.

Friends of FSH Research

Volunteer Run non-profit funding FSH Muscular Dystrophy research.

CMT Research Foundation Inc

The CMT Research Foundation has one mission: Deliver treatments and cures for #CMT.

• Specifically Named Diseases

• 43.

CTNNB1 Connect and Cure Inc

Connecting families, raising awareness, finding treatments and a cure for CTNNB1 Syndrome 🧬💛💙 https://t.

• Birth Defects, Genetic Diseases

• 44.

Therapies for Inherited Neuropathies Inc

Identifying and advancing research & therapies that bring solutions to CMT patients.

• Specifically Named Diseases Research

• 45.

Dion Foundation for Children with Rare Diseases Inc

Support research. Find a cure. Help children and families fight rare diseases.