• Neurology, Neuroscience

• 235.

Myelin Repair Foundation

The Myelin Repair Foundation's mission is to accelerate the availability of myelin repair treatments to improve the lives of people suffering from multiple sclerosis (MS).

• Single Organization Support

• 236.

INTERNATIONAL WAGR SYNDROME ASSOCIATION

The IWSA represents more than 350 members in 45 countries around the world The mission of the International WAGR Syndrome Association is to promote awareness, stimulate research, and support families affected by WAGR syndrome.

• Medical Disciplines

• 237.

Pediatric Neurotransmitter Disease Association Inc

The PND association is a disease organization representing children and families who are affected by a pediatric neurotransmitter disease.

WILLIAMS SYNDROME ASSOCIATION INC

WSA: research, programming and support for families and caregivers affected by Williams syndrome.

• Diseases, Disorders, Medical Disciplines N.E.C.

• 239.

RASOPATHIES NETWORK USA

A 501c3 organization; Our mission is to advance research of the #RASopathies by bringing stakeholders together.

• Birth Defects, Genetic Diseases Research

• 240.

Project Guardian

Project GUARDIAN Genomic Uniformscreening Against Rare Diseases In All Newborns Recent Interviews see more Revolutionizing Healthcare Dr.

• Specifically Named Diseases

• 241.

Extrapelvic Not Rare

Extrapelvic Not Rare is a grassroots non-profit organization, dedicated to advance awareness, education and prompt policy changes that leads to earlier recognition, reduced mis-, and delayed diagnosis of endometriosis that lies outside of the reproductive structures and local areas EPNR’s target audience includes healthcare disciplines and general public about endometriosis as a disease with body-wide potential.

• Birth Defects, Genetic Diseases

• 242.

HNRNP FAMILY FOUNDATION

Nonprofit dedicated to serving those impacted by HNRNP-Related Rare Neurodevelopmental Disorders through supporting community and research Home Donate Events Learn Projects Join our Registry Join our Researcher Registry Shop Contact and Connect Submit your story HNRNPC Item HNRNPH1RNDD HNRNPH2RNDD More Our Mission The HNRNP Family Foundation is dedicated to improving the lives of patients and families around the world that live with rare HNRNPRelated Neurodevelopmental Disorders HNRNPRNDDs.

• Fund Raising and/or Fund Distribution

• 243.

THE CHAMP FOUNDATION

Mission The Champ Foundation supports research toward better treatment and a cure for single largescale mitochondrial deletion syndromes SLSMDS like Pearson syndrome.