• Alliance/Advocacy Organizations

• 181.

PSC Partners Seeking a Cure

The mission of PSC Partners Seeking a Cure is to drive research to identify treatments and a cure for primary sclerosing cholangitis (PSC), while providing education and support for those impacted by this rare disease.

• Cancer Research

• 182.

Second Chance for Kids Foundation Inc

Our mission is to accelerate drug development for children with cancer by researching andinvestigating in drugs already in use and FDAapproved.

• Management & Technical Assistance

• 183.

Global Alzheimers Platform Foundation Inc

A non-profit organization building a unique network of researchers, volunteers, & communities focused on advancing Alzheimer’s and Parkinson's disease research.

• Specifically Named Diseases

• 184.

Prion Alliance Inc

Non-profit organization devoted to funding scientific research towards a treatment or cure for human prion diseases.

• Kidney

• 185.

PKD Foundation

Dedicated to finding treatments and a cure for polycystic kidney disease (PKD).

• Birth Defects, Genetic Diseases

• 186.

Shwachman-Diamond Syndrome Alliance Inc

Shwachman-Diamond Syndrome Alliance is a nonprofit aimed at accelerating research and therapy development for this rare disease.

Pacs1 Syndrome Research Foundation

THE GOAL OF THE PACS1 SYNDROME RESEARCH FOUNDATION IS TO FIND A TREATMENT FOR PACS1 SYNDROME (A DEBILITATING NEURO-GENETIC DISEASE) IN THE SHORTEST POSSIBLE TIME-FRAME BY FUNDING CUTTING-EDGE SCIENTIFIC RESEARCH About Us Contact Registry Scientific Advisory Board Funded Research More Funding Scientific Research to find Treatments for PACS1 Syndrome JOIN US DONATE AND MAKE A DIFFERENCE TODAY.

• Fund Raising and/or Fund Distribution

• 188.

Believe in A Cure, Inc.

Believe in a Cure, Inc. is a 501(c)(3) tax-exempt organization whose mission is to: (1) support the care and treatment of individuals diagnosed with FOXG1 Syndrome and similar disorders, as well as to raise public awareness regarding such issues; and (2) support research and development of learnings and methods to improve the qualify of life for patients with such disorders.

• Birth Defects, Genetic Diseases

• 189.

n-Lorem Foundation

Discovering, developing, and providing personalized experimental ASO medicines to treat nano-rare patients — for free, for life Creating a better future for nano-rare, one patient at a time.