• Specifically Named Diseases Research

• 145.

Muscular Dystrophy Association

MDA is the #1 voluntary health organization in the United States for people living with #MuscularDystrophy, #ALS, and related #neuromuscular diseases.

JETT FOUNDATION INC

Empowering families. Fighting Duchenne muscular dystrophy.

• Specifically Named Diseases Research

• 147.

Coalition Duchenne

We're on a mission to do everything FUN to raise global awareness for Duchenne muscular dystrophy, to fund research for a cure.

• Diseases, Disorders, Medical Disciplines N.E.C.

• 148.

LYMPHANGIOMATOSIS & GORHAMS DISEASE ALLIANCE INC

Patient-driven solutions for complex lymphatic anomalies: GLA, GSD, KLA, CCLA • Support-Research-Education • Somatic mutations PIK3/mTor & RAS/MAPK pathways Patient advocacy group dedicated to patient driven solutions for complex lymphatic anomalies We connect patients and families to peers and networks of care, partner to advance new research, and educate the medical community to help all people navigating complex lymphatic anomalies have hope for a healthier tomorrow.

• Fund Raising and/or Fund Distribution

• 149.

Emily's Entourage

Accelerating lifesaving research and drug development for the final 10% of people with #cysticfibrosis that don't benefit from mutation-targeted therapies.

• Fund Raising and/or Fund Distribution

• 150.

Curears A NJ Nonprofit Corporation

Our mission is to spread awareness, connect and provide support to affected families and fund research for the ultra-rare mtARS genes.

• Specifically Named Diseases

• 151.

Susan and Charles Berghoff Foundation

Our mission is to increase dementia education, caregiving resources and research, with a special focus on Lewy body disease, the second leading cause of neurodegenerative dementia after Alzheimer's disease.

• Public Foundations

• 152.

THE CHILDREN'S HEART FOUNDATION

Funding the most promising congenital heart defect research so that Heart Warriors everywhere can live longer, healthier lives.

• Birth Defects, Genetic Diseases

• 153.

THINKGENETIC FOUNDATION INC

Helping those living with a genetic disease by shortening the time to diagnose a genetic condition and providing actionable, patient-focused guidance.