Foundation for Angelman Syndrome Therapeutics

FAST is the premier patient advocacy organization working to cure Angelman syndrome.

• Nerve, Muscle, and Bone Diseases

• 119.

Cohen Syndrome Association

Welcome to the Official fan page of the Cohen Syndrome Association ®.

• Specifically Named Diseases

• 120.

Prion Alliance Inc

Non-profit organization devoted to funding scientific research towards a treatment or cure for human prion diseases.

Hope4Harper

Hope4Harper is a grassroots organization designed to provide hope to those living with CDKL5 deficiency and other seizure disorders by fostering awareness and supporting research.

Alpha-1 Foundation, Inc.

Our mission is to increase awareness of and find a cure for Alpha-1 Antitrypsin Deficiency.

• Health (General and Financing)

• 123.

Little Zebra Fund

Universal access to clinical genetic testing.

Myhre Syndrome Foundation

Myhre Syndrome Foundation is dedicated to serving Myhre syndrome families by providing a network of hope and support.

• Fund Raising and/or Fund Distribution

• 125.

THE YAYA FOUNDATION FOR 4H LEUKODYSTOPHY

Fighting for children and families affected by 4H Leukodystrophy.

• Public Foundations

• 126.

CURING RETINAL BLINDNESS

Welcome to our mission of bringing sight to children who are blind or visually impaired due to CRB1 retinal disease.