Moonshots for Unicorns

Overview

Moonshots for Unicorns is a US-based 501(c)(3) nonprofit organization focused on curing rare genetic disorders, such as PGAP3, by raising funds, coordinating and sponsoring research, spreading awareness, and advocating for affected families[1][5]. The organization was founded by parents who have a child with PGAP3 disorder, a rare condition affecting gene expression in every cell of the body[2].

Mission and Activities

The mission of Moonshots for Unicorns is to ensure that no parent faced with a diagnosis of a rare genetic disorder feels helpless. The organization aims to accelerate the development of treatments and potential cures by funding research and creating innovative approaches to drug repurposing[1][2]. They operate a pop-up laboratory where they test FDA-approved drugs for repurposing to delay or mitigate the effects of these disorders. This approach is particularly significant for conditions like PGAP3, which can lead to severe intellectual disability, lack of speech, and untreatable seizures[1][2].

Financial Status and Support

As of recent reports, Moonshots for Unicorns has generated substantial support, both financially and through community engagement. Their fundraising efforts have been robust, with notable success in rallying public support and donations[1][4]. By the end of 2023, the organization reported revenue of $144,000 and expenses of $70,300, with total assets valued at $329,000[4].

Community Impact and Legacy

Moonshots for Unicorns not only works to improve the lives of those affected by rare genetic disorders but also serves as a model for other organizations tackling similarly challenging conditions. The organization highlights the power of community-driven efforts and the need for innovative solutions in the field of genetic diseases[1]. Through its mission, Moonshots for Unicorns embodies a broader goal of providing hope to families dealing with rare and often incurable conditions[1][2].