Elamipretide has demonstrated real impact. The FDA has had the data. They’ve had the time. What they haven’t done is act. It’s unconscionable. This administration has said it supports rare disease families. Now is the moment to prove it. We need strong, decisive leadership. This is life and death. Read our statement and the stories behind the science: https://bit.ly/4mCZEh8 @fda U.S. Food and Drug Administration #GiftOfProgress #ApproveElamipretide #HopeForBarth #RareDisease #FDAActNow (fb)

💊 “The Drug That Gave Me My Life Back” Walker knows what life without elamipretide feels like—and what it feels like with it. For 7 years, this therapy transformed his day-to-day. Now, the FDA is stalling. Walker says it best: “This drug works. I’ve lived it.” Read the full story here 👉 bit.ly/44WRc6m @fda U.S. Food and Drug Administration @everylifeorg EveryLife Foundation for Rare Diseases @nord_rare National Organization for Rare Disorders, Inc. (NORD) #GiftOfProgress #ApproveElamipretide #HopeForBarth #RareDisease #FDAActNow (fb)