Charlie was one of the first U.S. participants in a phase 3 gene therapy clinical trial for Duchenne muscular dystrophy (DMD)—a rare, progressive condition that affects young boys. Thanks to early diagnosis and access to research, Charlie is now a proud third grader who loves the outdoors and shares his story with classmates to raise awareness about DMD. 💪 Learn how research is changing lives: https://urmc.info/clinicaltrials25 #ClinicalTrialsDay #ClinicalTrialsDay2025 #CTD2025 #URochesterResearch (fb)

At just 16, Mary Sarah became one of the first patients at Golisano Children's Hospital to receive therapeutic hypothermia through a national clinical trial, a treatment that cools the body to protect the brain after cardiac arrest. Now, she’s preparing for college—a powerful reminder of how research can save lives: https://urmc.info/clinicaltrials25 (fb)