In loving memory of a member of our AHC family, Luke Joseph. Gone much too soon. We will not forget you. We will continue to fight AHC in honor of you, Luke Joseph. 🖤 #together #inlovingmemory #endAHC #cureAHC (fb)

A Breakthrough for Rare Disease Families. Baby KJ recently became the first to receive CRISPR base editing treatment — and it worked! This is a historic moment for the rare disease world, including families impacted by AHC. It shows what’s possible when cutting-edge science meets unwavering hope. AHC already has research underway led by Nina English Frost exploring gene-targeted treatments, including CRISPR. Wishing Baby KJ a happy, healthy journey — and thanking their story for continuing hope for us all (fb)