• Birth Defects, Genetic Diseases

NATIONAL TAY SACHS & ALLIED DISEASES ASSOCIATION INC

National Tay-Sachs & Allied Diseases Association (NTSAD) leads the worldwide fight to treat and cure Tay-Sachs, Canavan, GM1, and Sandhoff diseases.

• Other Medical Research N.E.C.

NATIONAL TAY SACHS AND ALLIED DISEASES ASSOC OF DELAWARE VALLEY

NTSAD-DV provides free screening for Tay-Sachs and Canavan Dont make your next baby a sitting duck.

• Birth Defects, Genetic Diseases Research

SMS Research Foundation

The mission of the Smith-Magenis Syndrome Research Foundation is to advance scientific research leading to innovative treatment options for people living with SMS.

• Birth Defects, Genetic Diseases

Curefa Foundation Inc

CUREFA FOUNDATION FUNDS CAPITAL INTENSIVE PROJECTS GATED WITH SUCCESS MILESTONES, LEVERAGING NOVEL TOOLS OF SCIENTIFIC RESEARCH FOR THE TREATMENT AND CURE OF FRIEDREICH'S ATAXIA.

• Specifically Named Diseases

Wylder Nation Foundation

WARRIORS in the Fight Against Lysosomal Storage Disorders.

Malan Syndrome Foundation Inc

Malan syndrome is a rare genetic disorder that is the result of a change in the NFIX gene.

NEW HOPE RESEARCH FOUNDATION

The New Hope Research Foundation is a non-profit organization dedicated to: - Finding a genetic cure for GM2 gangliosidosis and other lysosomal storage diseases that affect the central nervous system, and - Providing hope to patients and their families currently facing the degenerative and debilitating aspects of these diseases.

• Epilepsy

Taylen Lauren Horton Foundation Inc

he Taylen Lauren Horton Foundation was created to not only bring awareness to Dravet Syndrome but to serve as a resource for providing information, motivation and inspiration to current families of children with Dravet Syndrome or those on the spectrum.

• Alliance/Advocacy Organizations

Baker-Gordon Syndrome Foundation

The BakerGordon Syndrome Foundation was founded to help families affected by this syndrome make connections with one another.

• Nerve, Muscle, and Bone Diseases

Cure VCP Disease Inc

Promoting a cure for diseases related to mutations of the Valosin Containing Protein gene ABOUT US FOR PATIENTS FOR RESEARCHERS FOR CLINICIANS EVENTS BLOG GIVE SHOP MORE Finding a cure is in our DNA Cure VCP Disease Inc.